Alzheimer's disease (AD) is a progressive neurodegenerative condition afflicting millions of patients worldwide. The disease is characterized by accumulation of amyloid-β (Aβ) peptides and hyperphosphorylated tau proteins in the brain resulting in neuronal loss and cognitive decline. The tau protein is an intrinsically disordered protein (IDP) that has diverse and crucial neuronal functions, including post-synaptic signalling in the mature brain. Tau is a promising target for the development of novel therapeutics to treat Alzheimer’s Disease; however, it’s intrinsically disordered nature makes the identification of interaction partners and the development of small molecule therapeutics a major challenge.
To address this problem, we have developed an integrated drug discovery platform that uses tau peptides engineered for protein-peptide interface dependent covalent crosslinking. We demonstrate that this platform can aid drug discovery through three key steps:
This Drug Discovery platform resolves a key hurdle in the development of new drugs with novel mechanisms of action for the treatment of Alzheimer’s Disease, with potential further application in drug discovery for other neurodegenerative diseases and non-neuroscience fields.